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Key highlights
  • Ten ATTR patients (mean age 63.8 years) received inotersen or patisiran at University Health Network.
  • 90% showed cardiac improvement on PYP scans; 1 patient worsened.
  • Serial PYP scintigraphy may provide an objective tool to monitor treatment response in ATTR.
Source

Arivalagan P, Delgado DH. Comparative study on cardiac findings in patients with transthyretin amyloidosis before and after treatment with a transthyretin silencer. J Cardiovasc Dev Dis. 2025;12(9):342. doi:10.3390/jcdd12090342

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TTR silencers linked to cardiac improvement in amyloidosis patients
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Short Description

Retrospective analysis finds improvements in PYP scan results and cardiac function in amyloidosis patients treated with inotersen or patisiran.

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